Study Details To evaluate efficacy and safety of oral, twice daily iptacopan in adult PNH patients who are naïve to complement inhibitor therapy
Protocol Number CLNP023C12301
Phase III
Therapeutic Area Haematology
Subject Types With Medical Condition
Indication Paroxysmal Nocturnal Hemoglobinuria (PNH)
Principal Investigator Dr Yap Eng Soo
Investigator Product / Device iptacopan
Sponsor Novartis (Singapore) Pte Ltd
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